HU, Ruiqin. Clinical Applications of Adeno-Associated Virus Gene Therapy in Rare Diseases. Highlights in Science, Engineering and Technology, [S. l.], v. 69, p. 650–656, 2023. DOI: 10.54097/hset.v69i.13779. Disponível em: https://drpress.org/ojs/index.php/HSET/article/view/13779. Acesso em: 3 jul. 2026.